Publications

Transthyretin Amyloidosis (ATTR)

Vutrisiran-Mediated Knockdown of Transthyretin in Patients with ATTR Amyloidosis

Clinical Pharmacokinetics

Author(s)

Marianna Fontana, Vincent Algalarrondo, Pablo Garcia-Pavia, et al

Transthyretin Amyloidosis (ATTR)

Vutrisiran in East Asian Patients With Transthyretin Amyloidosis With Cardiomyopathy: Post-Hoc Analysis of HELIOS-B

JACC: Asia

Author(s)

Jin Endo, Tetsuo Minamino, Jaewon Oh, et al

Transthyretin Amyloidosis (ATTR)

Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy and Renal Impairment: Analyses From HELIOS-B

Journal of Cardiac Failure

Author(s)

Farooq H. Sheikh, Julien Dang, Marianna Fontana, et al

Transthyretin Amyloidosis (ATTR)

Best Practices and Key Barriers for Amyloidosis Patient Care at US Specialized Amyloidosis Centers: An Analysis by ARC-ASPIRE

Clinical Medicine Insights: Cardiology

Author(s)

Jose Nativi-Nicolau, Johana Fajardo, Alyssa Galloway, et al

Transthyretin Amyloidosis (ATTR)

Effect of vutrisiran on components of health status in transthyretin amyloidosis with cardiomyopathy: the HELIOS-B study

European Journal of Heart Failure

Author(s)

Yasuhiro Hamatani, Brian L Claggett, Muthiah Vaduganathan, et al

Transthyretin Amyloidosis (ATTR)

Efficacy and Safety of Vutrisiran in Patients with Hereditary Transthyretin-mediated Amyloidosis with Polyneuropathy: Analysis of the East Asian Subpopulation from HELIOS-A

Neurology and Therapy

Author(s)

Jeeyoung Oh, Yoshiki Sekijima, Hideki Mochizuki, et al

Primary Hyperoxaluria Type 1 (PH1)

Final Results of the ILLUMINATE-A Phase 3 Clinical Trial of Lumasiran for Primary Hyperoxaluria 1

Clinical Journal of the American Society of Nephrology

Author(s)

Yaacov Frishberg, Jeffrey M. Saland, John Lieske, et al

Transthyretin Amyloidosis (ATTR)

Efficacy and safety of vutrisiran in transthyretin amyloid cardiomyopathy across the age spectrum: The HELIOS-B trial

European Journal of Heart Failure

Author(s)

Awais Sheikh, Zi Michael Miao, Brian Claggett, et al

Transthyretin Amyloidosis (ATTR)

Effectiveness and Utility of Genetic Testing in Establishing a Diagnosis of Hereditary Transthyretin Amyloidosis

Journal of Clinical Medicine

Author(s)

Akash Singh, John Wyatt, Marie Théaudin, et al

Transthyretin Amyloidosis (ATTR)

Impact of Patisiran on Polyneuropathy of Hereditary Transthyretin Amyloidosis in Patients with a V122I or T60A Variant: A Phase IV Multicenter Study

Annals of Medicine

Author(s)

Yessar Hussain, Saurabh Malhotra, Brett W. Sperry, et al