Publications

Transthyretin Amyloidosis (ATTR)

Effects of Vutrisiran on Cardiac Function and Outcomes in Patients With Transthyretin Amyloidosis With Cardiomyopathy

Journal of the American College of Cardiology

Author(s)

Karola S. Jering, Marianna Fontana, Hicham Skali, et al

Transthyretin Amyloidosis (ATTR)

Benefits of Patisiran on Functional Capacity in ATTR Cardiac Amyloidosis: Post Hoc Analysis of APOLLO-B

JACC: Advances

Author(s)

John L Berk, Olivier Lairez, Pedro Schwartzmann, et al

Transthyretin Amyloidosis (ATTR)

Realizing the therapeutic potential of rapid knockdown of transthyretin via RNA interference in transthyretin amyloidosis

Molecular Therapy Nucleic Acids

Author(s)

Martha Grogan, Farooq H. Sheikh, Brett W. Sperry, et al

Cardiovascular (CV)

Add-on Treatment With Zilebesiran for Inadequately Controlled Hypertension: The KARDIA-2 Randomized Clinical Trial

Journal of the American Medical Association

Author(s)

Akshay S. Desai, Adam D. Karns, Jolita Badariene

Transthyretin Amyloidosis (ATTR)

Vutrisiran Improves Survival and Reduces Cardiovascular Events in ATTR Amyloid Cardiomyopathy: HELIOS-B

Journal of the American College of Cardiology

Author(s)

Ronald Witteles, Pablo Garcia-Pavia, Thibaud Damy, et al

Transthyretin Amyloidosis (ATTR)

Treatment with vutrisiran in people with transthyretin amyloidosis with cardiomyopathy: A plain language summary

Future Cardiology

Author(s)

Marianna Fontana, Julian D Gillmore, Ronald M Witteles, et al

Primary Hyperoxaluria Type 1 (PH1)

Efficacy and Safety of Lumasiran for Advanced Primary Hyperoxaluria Type 1: 24-Month Follow-Up of the Phase 3 Illuminate-C Trial

American Journal of Kidney Diseases

Author(s)

Anne-Laure Sellier-Leclerc, Daniella Magen, Hadas Shasha-Lavsky, et al

Transthyretin Amyloidosis (ATTR)

Diagnosis of hereditary transthyretin amyloidosis in patients with suspected chronic inflammatory demyelinating polyneuropathy unresponsive to intravenous immunoglobulins: results of a retrospective study

Orphanet Journal of Rare Diseases

Author(s)

Yann Péréon, David Adams, Jean-Philippe Camdessanché, et al

Transthyretin Amyloidosis (ATTR)

Impact of Vutrisiran on Functional Capacity and Quality of Life in Transthyretin Amyloidosis with Cardiomyopathy

Journal of the American College of Cardiology

Author(s)

Farooq H. Sheikh, Gilbert Habib, W. H. Wilson Tang, et al

Transthyretin Amyloidosis (ATTR)

Impact of Heart Failure Severity on Vutrisiran Efficacy in Transthyretin Amyloidosis with Cardiomyopathy

Journal of the American College of Cardiology

Author(s)

Mathew S. Maurer, Ronald M. Witteles, Pablo Garcia-Pavia, et al