Publications
Transthyretin Amyloidosis (ATTR)
Six-minute walk test as clinical end point in cardiomyopathy clinical trials, including ATTR-CM: a systematic literature review
Journal of Comparative Effectiveness Research
Transthyretin Amyloidosis (ATTR)
Impact of Baseline Neuropathy Severity on Vutrisiran Treatment Response in the Phase 3 HELIOS-A Study
Neurology and Therapy
Transthyretin Amyloidosis (ATTR)
Patisiran, an RNAi therapeutic for hereditary transthyretin-mediated amyloidosis: Sub-analysis in Taiwanese patients from the APOLLO study
Journal of the Formosan Medical Association
Transthyretin Amyloidosis (ATTR)
Impact of vutrisiran on exploratory cardiac parameters in hereditary transthyretin-mediated amyloidosis with polyneuropathy
European Journal of Heart Failure
Transthyretin Amyloidosis (ATTR)
Patisiran Treatment in Patients with Transthyretin Cardiac Amyloidosis
New England Journal of Medicine
Transthyretin Amyloidosis (ATTR)
Pharmacokinetics and Pharmacodynamics of Patisiran in Patients with hATTR Amyloidosis and with Polyneuropathy After Liver Transplantation
Clinical Pharmacokinetics
