Publications

Transthyretin Amyloidosis (ATTR)

Effects of Patisiran, an RNA Interference Therapeutic, on Cardiac Parameters in Patients With Hereditary Transthyretin-Mediated Amyloidosis

Circulation

Author(s)

Scott Solomon, David Adams, Arnt Kristen, et al

Acute Hepatic Porphyria (AHP)

Patient Perspective on Acute Intermittent Porphyria with Frequent Attacks: A Disease with Intermittent and Chronic Manifestations

The Patient: Patient-Centered Outcomes Research

Author(s)

Amy Simon, Farrah Pompilus, William Querbes, et al

Transthyretin Amyloidosis (ATTR)

Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis

New England Journal of Medicine

Author(s)

David Adams, Alejandra Gonzalez-Duarte, William O’Riordan, et al