Publications
Acute Hepatic Porphyria (AHP)
Efficacy and safety of givosiran for acute hepatic porphyria: Final results of the randomized phase III ENVISION trial
Journal of Hepatology
Acute Hepatic Porphyria (AHP)
Pharmacokinetic-Pharmacodynamic Model of Urinary δ-Aminolevulinic Acid Reduction After Givosiran Treatment in Patients with Acute Hepatic Porphyria
CPT: Pharmacometrics & Systems Pharmacology
Acute Hepatic Porphyria (AHP)
Population Pharmacokinetic Analysis of the RNAi Therapeutic Givosiran in Patients with Acute Hepatic Porphyria
Clinical Pharmacokinetics
Acute Hepatic Porphyria (AHP)
EXPLORE B: A prospective, long-term natural history study of patients with acute hepatic porphyria with chronic symptoms
Journal of Inherited Metabolic Disease
Acute Hepatic Porphyria (AHP)
Hyperhomocysteinemia in acute hepatic porphyria (AHP) and implications for treatment with givosiran
Expert Review of Gastroenterology & Hepatology
